Browse by Murdoch Affiliation
- Murdoch University (5)
- Health Futures Institute (5)
- Centre for Molecular Medicine and Innovative Therapeutics (5)
- Health Futures Institute (5)
2022
Keegan, Niall Patrick (2022) Hidden stitches: RNA cryptic splicing and its role in human disease. PhD thesis, Murdoch University.
2021
Cale, Jessica M. (2021) Antisense oligonucleotide-mediated alternative splicing strategies to treat the type-1 fibrillinopathies. PhD thesis, Murdoch University.
Grainok, Janya (2021) Development of molecular therapies for retinitis pigmentosa 11. PhD thesis, Murdoch University.
Huang, Di (2021) Characterizing Stargardt disease-causing mutations to identify ABCA4 gene lesions amenable to splice intervention therapeutics. PhD thesis, Murdoch University.
2020
McIntosh, Craig Stewart (2020) Antisense oligonucleotide-mediated therapeutic strategies for neurodegenerative repeat expansion diseases. PhD thesis, Murdoch University.